According to the FDA's Center for Biologics Evaluation and Research, gene therapy is the use of normal genes or genetic material to replace or cancel out the "bad" or defective genes in a person's body that are responsible for a disease or medical problem. In early studies of gene therapy for cancer, researchers were trying to improve the body's natural ability to fight the disease or to make the tumor more sensitive to other kinds of therapy. This treatment may involve the addition of a functional gene or group of genes to a cell by gene insertion to correct a hereditary disease.
Glossary
Gene Therapy
02.27.12
-
-
Bio News | Biologics, Proteins, Vaccines | Breaking News | Industry News
Andelyn Biosciences, Odylia Therapeutics Partner to Manufacture Gene Therapy for Vision Loss
Novel AAV capsid Anc80 enables efficient gene transfer.
-
Breaking News | Promotions & Moves
Exothera Names Darren Leva as Chief Business Officer
Leva brings 20 years of broad commercial expertise to Exothera from a range of experiences with CDMOs, therapeutics, and software companies.
-
Biologics, Proteins, Vaccines | Breaking News | Industry News
New CDMO Vector BioMed Launches Operations
The biomanufacturing company’s mission is to provide access to high-quality lentiviral vectors and address the vector supply bottleneck.
-
Biologics, Proteins, Vaccines | Breaking News | cGMP Manufacture | Industry News
Lonza Further Invests in Drug Product Manufacturing Capabilities
New filling line to process various modalities, including monoclonal antibodies, bioconjugates, viral vectors, and other gene therapy products.
